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RNA Actuators · Programmable Therapeutics · Publications & Presentations ·
January 25, 2024
Scientific Reports

Transcriptional characterization of iPSC-derived microglia as a model for therapeutic development in neurodegeneration

December 14, 2023
Keystone Symposia Regulatory RNAs: Emerging Mechanisms

Antisense oligonucleotide therapeutic candidates targeting regulatory RNAs to treat urea cycle disorders

December 6, 2023
Nucleic Acids Research

JMnorm: a novel joint multi-feature normalization method for integrative and comparative epigenomics

October 18, 2023
Nature Conferences Cracking the Code: The Dawn of Nucleic Acid Medicines

Enhancer identification using machine learning enables efficient enhancer RNA targeting with antisense oligonucleotide-based therapeutics

October 18, 2023
Nature Conferences Cracking the Code: The Dawn of Nucleic Acid Medicines

Antisense oligonucleotide therapeutic candidates targeting regulatory RNAs to treat urea cycle disorders

August 6, 2023
Chromatin and Regulation of Gene Expression, Penn State’s 39th Summer Symposium in Molecular Biology

JMnorm: a novel Joint Multi-feature normalization method for integrative and comparative epigenomics

May 7, 2023
TIDES USA Oligonucleotide & Peptide Therapeutics conference

Antisense oligo targeting of GRN regulatory RNA upregulates progranulin: a potential therapeutic approach for granulin-related frontotemporal dementia

March 14, 2023
Cold Spring Harbor Network Biology meeting

JMnorm: a novel method for Joint Multi-feature normalization of epigenomic data

November 7, 2022
AASLD The Liver Meeting 2022

Upregulation of a bile acid regulator by targeting regulatory RNAs can enhance hepatic bile acid efflux in PBC

October 26, 2022
ASHG 2022 Annual Meeting

Linking GWAS risk variants to disease genes by epigenomic mapping and prediction of functional enhancer-promoter interactions

October 2, 2022
18TH ANNUAL MEETING OF THE OLIGONUCLEOTIDE THERAPEUTICS SOCIETY

Targeting regRNAs with oligonucleotides to treat OTC deficiency

October 2, 2022
18TH ANNUAL MEETING OF THE OLIGONUCLEOTIDE THERAPEUTICS SOCIETY

Upregulation of SerpinG1 for treatment of hereditary angioedema using RNA actuators

April 25, 2022
DIA/FDA Oligonucleotide-Based Therapeutics Conference

Upregulation of SCN1A by regRNA-Targeting Antisense Oligonucleotide CMP-SCN

March 11, 2022
Cold Spring Harbor Laboratory 15th Annual Global Regulation of Gene Expression Conference

Accurate Prediction of Functional Enhancer-Promoter Interactions Using Epigenomic Data

December 3, 2021
American Epilepsy Society Annual Meeting

SCN1A Upregulation via Antisense Oligonucleotides Targeting SCN1A-NAT as a Novel Therapeutic Strategy for Dravet Syndrome

November 18, 2021
30th Annual Irwin Arias symposium

A Novel Treatment Approach For Treating OTC Deficiency By Targeting RegRNAs Using Oligonucleotides

September 26, 2021
17TH ANNUAL MEETING OF THE OLIGONUCLEOTIDE THERAPEUTICS SOCIETY

A Novel Treatment Approach For Treating OTC Deficiency By Targeting RegRNAs Using Oligonucleotides

September 26, 2021
17th Annual Meeting of the Oligonucleotide Therapeutics Society

Oligonucleotide Upregulation of Serping1 by Targeting Regulatory RNAs

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